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Abbey Meyers Khushi
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2024
2023
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Our Speakers
Keynote Speakers
Amrit Ray, MD, MBA
Biopharma Executive, Rare Parent
David A Pearce PhD
Chair
International Rare Disease Research Consortium (IRDiRC)
Peter Marks, MD, PhD
Director
Center for Biologics Evaluation and Research (CBER) FDA
Dr. L Swasticharan
Additional DDG and Director (EMR)
Directorate General of Health Services Ministry of Health and Family Welfare, Govt of India
Vikram Karnani, MS, MBA
Executive Vice President and President, Global Commercial Operations and Medical Affairs
Horizon Therapeutics
Special Address
Abbey S Meyers, PhD
Founder and past President
National Organization for Rare Disorders (NORD)
Keynote Speakers
John F. Crowley
Biotechnology Innovation Organization (BIO)
Rakesh K. Mishra, PhD
Tata Institute for Genetics and Society (TIGS)
Victoria Gamerman, PhD
RWD Insights
Vijay Kumar, MD
Office of Therapeutic Products CBER/FDA
Our Speakers
Anand Swaroop, PhD
NEI
Anish Bhatnagar, MD
IndoUSrare and Soleno Therapeutics
Amy Adams, Ph.D.
Institute for Biohealth Innovation, George Mason University
Bijaya Mishra,MD
BPKIHS,Nepal
Brian Tseng, MD, PhD
PolG Foundation
Bushra Afroze, MBBS, DCH, MCPS, FCPS
The Aga Khan University Hospital
Caitlyn Barrett, PhD
Milken Institute SPARC
Christopher P. Boone, PhD, FACHE, FHIMSS
Oracle Corporation
David Rintell, EdD
BridgeBio
Del Smith, PhD
Acclinate
Donney John, PharmD
NOVA ScriptsCentral
Dr. Bobby Mukkamala, MD
Board of Directors, American Medical Association
Dr. Ratna Devi
Dakshayani and Amaravati Health and Education
Erika Torjusen, MD, MHS
Office of Orphan Products Development (OOPD), US FDA
Frank Sasinowski, JD, MPH
IndoUSrare and Hyman Phelps McNamara PC
Gerald Farrokh Daneshvar, MD
Ainsley Advisory Group
Gurdyal Kalsi, MD, MFPM (Hon), AskBio Consult
Asklepion Pharmaceuticals
Himanshu Kansara
TheGoodAI
Hemang Maniar
Duke Clinical Research Institute (DCRI)
Isaac R. Rodriguez-Chavez, PhD, MHSc, MSc
4Biosolutions Consulting
Jamie Sullivan, MPH
Every Life Foundation for Rare Diseases*
Jennifer Farmer, MS
Friedreich's Ataxia Research Alliance
Jenifer Waldrop, MSHRD
Rare Disease Diversity Coalition (RDDC)
Jill Yersak, PhD
Soleno Therapeutics
John Newby, JD
Virginia Bio
Juhi Naithani, MBA
IndoUSrare and bGlobal Consulting
Julienne M. Vaillancourt, RPh, MPH
CBER, US FDA
Kapil Patel
Inspiring Happiness At Work
Karla MacDonald
Entrada Therapeutics
Krishna Madiraju
Century Pediatrics Inc
Kuntal Sen, MD
Childrens National Hospital, Washington, DC
K Thangaraj, PhD
CCMB-TIGS Outstanding Scientist
Lara Bloom
The Ehlers-Danlos Society
Lisa Shea, BA, LLB, JD
Immigrants First, PLLC
Madhulika Kabra, MD
Indian Council for Medical Research
Mathew T Thomas, MBBS
IndoUSrare and former USFDA India Office Country Director
Mandeep Kaur, MD, MS
Valion Consulting
Mohamed Duklef, RPh, M.Sc.
Center for Orphan Drug Research (CODR), UMN
Monica Dudley-Weldon, BS, MSL
VA Commonwealth Health Research Board (CHRB) Appointee
Nandita Roy
Narendra Chirmule, PhD
Symphony Technologies
Neerja Gupta, MD, DM
All India Institute of Medical Sciences, New Delhi
Nishitha Pillai, MD
University of Minnesota
Parva Purohit, PhD
Amneal Pharmaceuticals
Pesh Patel
A Kidney Life
Prof Sheffali Gulati, MD, FRCPCH (UK), FAMS, FIAP, FIMSA
All India Institute of Medical Sciences, New Delhi
Prof. Huma Cheema, MRCP, DPGN
University of Child Health, Lahore, Pakistan
Rajesh Gooty
Lead America Foundation
Community Champion Awardee
Ratna Dua Puri, MD, DM
Sir Ganga Ram Hospital
Reena Kartha, MS, PhD
IndoUSrare and Center for Orphan Drug Research, UMN
Rich Bendis
BioHealth Innovation and BioHealth Capital Region Forum
Sanket Shah, MD, PhD
Jazz Pharma
Sara Tylosky, MBA
Farmacon Global
Saikat Sarkar
Sambit Mohanty,MBA
Entero Healthcare Solutions Ltd
Scott K. Winiecki, MD
FDA
Sonit Handa, MD, MS, MBA
Biovance Consulting LLC
Sunitha Malepathi
CACNA1A Foundation
Terry Jo Bichell, PhD, MPH
COMBINEDBrain
Tina Aswani-Omprakash, MPH
South Asian IBD Alliance
Tshaka Cunningham PhD, Athari Bio
Polaris Genomics
Vaadiyar Madhusudhan (Madhu), PhD
LifeArc
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